THIRD EDITION
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Factsheets
These factsheets give basic information on the top 100 conditions that every student needs to know.
Chromosomal disorders
Trisomy 13
Trisomy 18
Trisomy 21
XXY
Turner syndrome
XYY
XXX
Velo-cardio-facial/DiGeorge syndrome
Prader-Willi syndrome
Angelman syndrome
Williams syndrome
Cancer Predispositon Syndromes
Cowden syndrome
Li-Fraumeni syndrome
Hereditary breast and ovarian cancer
Familial adenomatous polyposis
Hereditary nonpolyposis colon cancer
von Hippel-Lindau syndrome
Neurofibromatosis
Tuberous sclerosis complex
Multiple endocrine neoplasia
Retinoblastoma
Dermatologic disorders
Incontinentia Pigmenti
Ectodermal dysplasia
Albinism
Epidermolysis bullosa
Gastrointestinal disorders
Hemochromatosis
Wilson disease
Pulmonary disorders
Cystic fibrosis
α
1
-antitrypsin deficiency
Neurological disorders
Huntington disease
Holoprosencephaly
Hereditary ataxia
Fragile X syndrome
Rett syndrome
Canavan disease
Hereditary dystonia
Alzheimer disease
Autism
Ataxia-telangiectasia
Neuromuscular disorders
Spinal muscular atrophy
Duchenne/Becker muscular dystrophy
Myotonic dystrophy
Familial dysautonomia
Hereditary motor and sensory neuropathy
Hematological disorders
Hemoglobinopathies
Hereditary angioedema
Hemophilias
Thrombophilia
Hereditary hemorrhagic telangiectasia
DNA Repair disorders
Bloom syndrome
Xeroderma pigmentosum
Fanconi anemia
Congenital anomaly
Neural tube defect
CHARGE syndrome
Beckwith-Wiedemann
VACTERL association
Noonan syndrome
Progeria
Craniosynostosis
Hirschsprung disease
Renal/Genital Disorders
Polycystic kidney disease
Androgen insensitivity syndrome
Y chromosome infertility
Skeletal/Connective Tissue
Osteogenesis imperfecta
Marfan syndrome
Ehlers-Danlos syndrome
Achondroplasia
Endocrine Disorders
Congenital adrenal hyperplasia
Diabetes mellitus
Cardiovascular disorders
Cardiomyopathy
Holt-Oram syndrome
Long QT syndrome
Inborn Errors of Metabolism
Phenylketonuria
Maple syrup urine disease
Organic acidemia
Alkaptonuria
Adrenoleukodystrophy/peroxisomal disorders
Fatty acid oxidation disorders
Fabry disease
Gaucher disease
Niemann-Pick disease
Tay-Sachs disease
Menkes disease
Smith-Lemli-Opitz syndrome
Glycogen storage disease
Mucopolysaccharidosis
Urea cycle disorders
Familial hypercholesterolemia
Homocystinuria
Lesch-Nyhan syndrome
MELAS
MERFF
Leber hereditary optic neuropathy
Acute intermittent porphyria
Tangier disease
Galactosemia
Tyrosinemia
Sensory disorders
Hereditary deafness
Color blindness
Retinitis pigmentosum
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